The gene-editing treatment will be available to certain patients with sickle cell disease in England as Vertex commits to collecting additional data.
The most advanced engineering of human cell lines to date has been accomplished by scientists, demonstrating that genomes are more robust against significant structural changes than previously ...
The most complex engineering of human cell lines ever has been achieved by scientists, revealing that our genomes are more resilient to significant structural changes than was previously thought.
NHS officials estimate around 50 people a year will receive treatment now it has been approved for use for certain patients with severe sickle cell disease. | ITV National News ...
Experts hailed exciting news for some people with sickle cell disease in England as the health watchdog decided to grant ...
The National Institute for Health and Care Excellence (NICE) has approved Vertex Pharmaceuticals’ Casgevy (exagamglogene ...
The gene therapy Casgevy, which will now be offered to some patients in England, could help people live disease-free, experts ...
NHS officials estimate that around 50 people a year will receive treatment now that it has been approved for use for certain ...
Australian researchers have successfully introduced an improved version of Cas12a gene-editing enzyme in mice.
The company will use the funding to advance clinical trials for Tune-401, the epigenetic silencing drug for treating chronic ...
Design Therapeutics' GeneTAC platform is revolutionizing genetic disease treatment with small molecules and promising results ...